For ADA gene therapy, lymphocytes are grown in culture and ADA cDNA is introduced. Periodic replacement is necessary, but if done early, it can lead to a permanent cure.
En la terapia génica para la ADA, se cultivan linfocitos y se introduce ADNc de ADA. El reemplazo periódico es necesario, pero si se realiza en una etapa temprana, puede ser una cura permanente.
Front | how gene therapy for the ADA |
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Back | the lymphocyte is grown in a culture and ADA cDNA is indroduced -periodic replacement is necessary but if it is done in early stage then it will be a permanet cure |
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